Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD)
Summary
The lay summary the sponsor registered on ClinicalTrials.gov.
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Ana Camacho Salas, MD
Hospital Universitario 12 de Octubre
Principal Investigator - Ass. Prof. Jan Verschuuren, MD, PhD
Leiden University Medical Center (LUMC), 2300 RC Leiden, the Netherlands
Principal Investigator - Barry Byrne, MD
University of Florida
Principal Investigator - Bryan W. Burnette, MD
Monroe Carell Jr. Children's Hospital at Vanderbilt
Principal Investigator - Craig McDonald, MD
University of California, Davis
Principal Investigator - Dr. Günther Bernert, Prim. Univ. Doz.
Vorstand der Abteilung für Kinder- und Jugendheilkunde, Gottfried v. Preyer'sches Kinderspital, 1100 Wien, Austria
Principal Investigator - Dr. Pierre-Yves Jeannet, Médecin Associé, MER
Unité de Neuropédiatrie, CHUV - BH11, 1011 Lausanne-CH, Switzerland
Principal Investigator - Dr. Ulrike Schara, MD, PhD
Universitätsklinikum Essen, D-45122 Essen, Germany
Principal Investigator - Ericka Simpson, MD
Methodist Neurological Institute, Houston
Principal Investigator - Gihan Tennekoon, MD
Division of Neurology - The Children's Hospital of Philadelphia - 34th Street and Civic Center Blvd, Philadelphia, PA 19104-1771, USA
Principal Investigator - Janbernd Kirschner, MD
Universitätsklinik Freiburg Zentrum für Kinderheilkunde und Jugendmedizin
Principal Investigator - Jean-Marie Cuisset, MD
Hôpital Roger Salengro, CHRU, Service de neurologie infantile, Lille, France
Principal Investigator - Juan Jesus Vilchez, MD
Hospital Universitari y Politècnic La Fe de Valencia
Principal Investigator - Ksenija Gorni, MD
Azienda Ospedaliera Niguarda Ca'Granda Centro Clinico Nemo
Principal Investigator - Luisa Politano, MD
Azienda Ospedaliera Universitaria della Seconda Università degli Studi di Napoli
Principal Investigator - Maria Grazia Nadia D'Angelo, MD
Fondazione IRCCS "Eugenio Medea"
Principal Investigator - Michele Yang, MD
Children's Hospital Colorado
Principal Investigator - Prof. Gunnar Buyse, MD, PhD.
University Hospitals Leuven, B-3000, Belgium
Principal Investigator - Prof. Thomas Sejersen, MD, PhD
Astrid Lindgrens Barnsjukhus- Karolinska Universitetssjukhuset, SE-17176 Stockholm, Sweden
Principal Investigator - Prof. Thomas Voit, MD, PhD
Université Pierre et Marie curie VI - Institut de Myologie - groupe hospitalier Pitié Salpétrière - 47/83 boulevard de l'hôpital, 75651 Paris Cedex 13, France
Principal Investigator - Susan Apkon, MD
Seattle Children's Hospital
Principal Investigator - Susan Iannaccone, MD
University of Texas Southwestern Medical Center, TX, USA
Principal Investigator - Susan Sparks, MD
The Charlotte-Mecklenburg Hospital Authority, Charlotte, NC, USA
Principal Investigator
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
23 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- Dr. Günther Bernert, Prim. Univ. Doz.
Vienna, Austria
- University Hospitals Leuven- Children Hospital
Leuven, Belgium
- Hôpital Roger Salengro, Chru Lille
Lille, France
- Prof. Thomas Voit , Md, Phd
Paris, France
- Universitätsklinikum Essen, Zentrum Für Kinderheikunde
Essen, Germany
- Universitätsklinik Freiburg Zentrum Für Kinderheilkunde Und Jugendmedizin
Freiburg im Breisgau, Germany
- Fondazione Irccs "eugenio Medea"
Bosisio Parini, Lecco, Italy
- Azienda Ospedaliera Niguarda Ca' Granda Centro Clinico Nemo
Milan, Italy
- Azienda Ospedaliera Universitaria Della Seconda Università Degli Studi Di Napoli
Naples, Italy
- Ass. Prof. Jan Verschuuren , Md, Phd
Leiden, P.O. Box 9600, Netherlands
- Hospital Universitario 12 de Octubre
Madrid, Spain
- Hospital Universitario Y Politécnico la Fe
Valencia, Spain
- Prof. Thomas Sejersen, Md, Phd
Stockholm, Sweden
- Chuv Lausanne Neuropediatrie
Lausanne, Switzerland
- University of California Davis Medical Center
Sacramento, California, United States
- Children'S Hospital Colorado
Aurora, Colorado, United States
- University of Florida
Gainesville, Florida, United States
- Carolinas Medical Center, Neurosciences and Spine Institute
Charlotte, North Carolina, United States
- the Children'S Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
- Monroe Carell, Jr. Children'S Hospital at Vanderbilt
Nashville, Tennessee, United States
- University of Texas Southwestern Medical Center
Dallas, Texas, United States
- Methodist Neurological Institute
Houston, Texas, United States
- Seattle Children'S Hospital
Seattle, Washington, United States
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
The drug and biological interventions registered on this study, normalized to their RxNorm ingredient where possible.
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 31 Jul 2009
- Primary completion
- 31 Jan 2014
- Completion
- 30 Apr 2014
- Last update posted
- 19 Oct 2015
- Registered enrollment
- 65
- Registry id
- NCT01027884
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 24 Aug 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.