A Phase 2 Study to Evaluate the Dose and Pharmacodynamic Efficacy of Sialic Acid-Extended Release (SA-ER) Tablets in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy
Summary
The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Alan Pestronk, MD
Washington University School of Medicine
Principal Investigator - Heather Lau, MD
NYU Langone Health
Principal Investigator - Perry Shieh, MD
University of California, Los Angeles
Principal Investigator - Yoseph Caraco, MD
Hadassah University Hospital
Principal Investigator
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
4 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- Hadassah University Hospital
Jerusalem, Israel
- Ucla Medical Center
Los Angeles, California, United States
- Washington University School of Medicine
St Louis, Missouri, United States
- New York University School of Medicine
New York, New York, United States
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 31 May 2012
- Primary completion
- 30 Nov 2013
- Completion
- 30 Nov 2013
- Last update posted
- 16 Jun 2016
- Registered enrollment
- 46
- Registry id
- NCT01517880
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.