Patients Treated for Wiskott-Aldrich Syndrome (WAS) Since 1990
Summary
The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Alexandra H. Filipovich, MD
Children's Hospital Medical Center, Cincinnati
Study Chair - David J. Rawlings, MD
Department of Pediatrics, University of Washington-Seattle Children's Hospital
Study Chair - Lauri M. Burroughs, MD
Fred Hutchinson Cancer Center
Study Chair - Luigi D. Notarangelo, MD
National Institute of Allergy and Infectious Diseases, NIH
Study Chair
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
43 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- Alberta Children'S Hospital
Calgary, Alberta, Canada
- Children'S & Women'S Health Centre of British Columbia
Vancouver, British Columbia, Canada
- Cancer Care Manitoba, University of Manitoba
Winnipeg, Manitoba, Canada
- the Hospital for Sick Children
Toronto, Ontario, Canada
- Chu Sainte-Justine, Department of Pediatrics, University of Montreal
Montreal, Quebec, Canada
- Department of Pediatrics, University of Alabama at Birmingham
Birmingham, Alabama, United States
- Phoenix Children'S Hospital
Phoenix, Arizona, United States
- Cancer and Blood Disease Institute, Children'S Hospital Los Angeles, Keck School of Medicine, University of Southern California
Los Angeles, California, United States
- Department of Pediatrics, David Geffen School of Medicine at University of California, Los Angeles,
Los Angeles, California, United States
- Lucile Salter Packard Children'S Hospital at Stanford
Palo Alto, California, United States
- University of California, San Francisco Benioff Children'S Hospital
San Francisco, California, United States
- Children'S Hospital Denver, University of Colorado
Denver, Colorado, United States
- Nemours Alfred I. Dupont Hospital for Children
Wilmington, Delaware, United States
- Children'S National Hospital-George Washington University School of Medicine and Health Sciences
Washington D.C., District of Columbia, United States
- Blood and Marrow Transplant Program, Johns Hopkins All Children'S Hospital
St. Petersburg, Florida, United States
- Aflac Cancer and Blood Disorders Center, Emory/children'S Healthcare of Atlanta
Atlanta, Georgia, United States
- Ann & Robert H. Lurie Children'S Hospital of Chicago
Chicago, Illinois, United States
- Center for Cancer and Blood Disorders, Children'S Hospital/louisiana State University
New Orleans, Louisiana, United States
- Boston Children'S Hospital
Boston, Massachusetts, United States
- Department of Pediatrics, C. S. Mott Children'S Hospital, University of Michigan
Ann Arbor, Michigan, United States
- Division of Pediatric Blood and Marrow Transplantation, University of Minnesota
Minneapolis, Minnesota, United States
- Mayo Clinic Children'S Center
Rochester, Minnesota, United States
- Cardinal Glennon Children'S Hospital, Saint Louis University
St Louis, Missouri, United States
- Saint Louis Children'S Hospital, Washington University
St Louis, Missouri, United States
- Institute for Pediatric Cancer and Blood Disorders, Hackensack University Medical Center
Hackensack, New Jersey, United States
- Department of Pediatrics, Memorial Sloan Kettering Cancer Center
New York, New York, United States
- Department of Pediatrics, Golisano Children'S Hospital, University of Rochester
Rochester, New York, United States
- Maria Fareri Children'S Hospital, New York Medical College
Valhalla, New York, United States
- Duke University Medical Center
Durham, North Carolina, United States
- Cincinnati Children'S Hospital Medical Center, University of Cincinnati
Cincinnati, Ohio, United States
- Rainbow Babies and Children'S Hospital
Cleveland, Ohio, United States
- Nationwide Children'S Hospital
Columbus, Ohio, United States
- Division of Pediatric Hematology/oncology, Oregon Health and Science University
Portland, Oregon, United States
- Children'S Hospital of Philadelphia, University of Pennsylvania
Philadelphia, Pennsylvania, United States
- University of Pittsburgh Children'S Hospital of Pittsburgh
Pittsburgh, Pennsylvania, United States
- St. Jude Children'S Research Hospital
Memphis, Tennessee, United States
- Pediatrics, University of Texas Southwestern Medical Center
Dallas, Texas, United States
- Baylor College of Medicine Section of Immunology, Allergy, and Retrovirology, Texas Children'S Hospital
Houston, Texas, United States
- Texas Transplant Institute, Methodist Children'S Hospital
San Antonio, Texas, United States
- Primary Children'S Hospital, University of Utah
Salt Lake City, Utah, United States
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 2 Feb 2014
- Primary completion
- 1 May 2019
- Completion
- 1 May 2019
- Last update posted
- 10 Aug 2020
- Registered enrollment
- 305
- Registry id
- NCT02064933
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.