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Clinical trialNCT02139306CompletedPhase 3Interventional

Study of Ataluren in Nonsense Mutation Cystic Fibrosis (ACT CF)

SponsorPTC TherapeuticsEnrollment279Cystic Fibrosis
View the registry record on ClinicalTrials.gov

Summary

The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →

Investigators

The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.

A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.

Sites

88 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.

Argentina
  • Hospital Universitario Austral

    Buenos Aires, Argentina

  • Hospital de Niños Dr. Ricardo Gutiérrez

    Buenos Aires, Argentina

  • Hospital de Niños Superiora Sor Maria Ludovica

    La Plata, Argentina

Australia
  • Royal Adelaide Hospital

    Adelaide, Australia

  • Prince Charles Hospital

    Chermside, Australia

  • Princess Margaret Hospital

    Perth, Australia

Belgium
  • Hôpital Universitaire Des Enfants Reine Fabiola

    Brussels, Belgium

  • University Hospital Brussels

    Brussels, Belgium

  • University Hospital Leuven

    Leuven, Belgium

Brazil
  • Hospital Sao Lucas Da Pontificia Universidade Catolica Do Rio Grande Do Sul

    Porto Alegre, Brazil

  • Instituto Da Criança - Hospital Das Clínicas

    São Paulo, Brazil

Bulgaria
  • University Mulitiprofile Hospital for Active Treatment Sveti Georgi Ead

    Plovdiv, Bulgaria

  • University Multiprofile Hospital for Active Treatment Aleksandrovska Ead

    Sofia, Bulgaria

Canada
  • Clinical Research Institute of Montreal

    Montreal, Canada

  • Chu de Quebec - Hopital Chul

    Québec, Canada

  • University of Toronto Hospital for Sick Children

    Toronto, Canada

  • British Columbia Children'S Hospital

    Vancouver, Canada

France
  • Hôpital Femme-Mère-Enfant

    Bron, France

  • Hôpital Arnaud de Villeneuve

    Montpellier, France

  • Hôpital Necker-Enfants Malades

    Paris, France

  • Centre de Perharidy

    Roscoff, France

  • Centre Hospitalier Regional Sud Reunion

    Saint-Pierre, France

Germany
  • Charité Universitätsmedizin Berlin

    Berlin, Germany

  • St. Josef Hospital Gmbh

    Bochum, Germany

  • Universitätsklinikum Köln

    Cologne, Germany

  • Christiane Herzog Cf-Zentrum

    Frankfurt am Main, Germany

  • Universitätsklinikum Jena

    Jena, Germany

  • Dr. Von Haunersches Kinderspital

    München, Germany

  • Lmu Klinikum Der Universität München

    München, Germany

Greece
  • General Hospital of Thessaloniki Ippokration

    Thessaloniki, Greece

Israel
  • Meyer Children'S Hospital

    Haifa, Israel

  • Hadassah University Hospital

    Jerusalem, Israel

Italy
  • Ospedali Riuniti Di Ancona

    Ancona, Italy

  • Azienda Ospedaliera A Meyer

    Florence, Italy

  • Lombardia Cystic Fibrosis Center

    Milan, Italy

  • Ospedale Pediatrico Bambino Gesù Irccs

    Roma, Italy

  • Azienda Policlinico Umberto I

    Rome, Italy

  • University of Verona

    Verona, Italy

Netherlands
  • Radboud University

    Nijmegen, Netherlands

  • Erasmus Mc

    Rotterdam, Netherlands

48 more sites on the registry record.ClinicalTrials.gov ↗

Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.

Drugs studied

No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →

Registration & key dates

Registry attributes as recorded on the ClinicalTrials.gov study record.

Start
31 Aug 2014
Primary completion
30 Nov 2016
Completion
30 Nov 2016
Last update posted
14 May 2020
Registered enrollment
279
Registry id
NCT02139306

Cross-registrations

EU-CTR / CTIS (EudraCT)2013-004581-34

Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.