A Study for Participants With Spinal Muscular Atrophy (SMA) Who Previously Participated in Nusinersen (ISIS 396443) Investigational Studies
Summary
The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Medical Director
Biogen
Study Director
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
47 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- Sydney Children'S Hospital Clinical Research Centre
Sydney, New South Wales, Australia
- Royal Children'S Hospital
Parkville, Victoria, Australia
- Universitair Kinderziekenhuis Koningin Fabiola
Brussels, Belgium
- Bc Children'S Hospital / Ubc
Vancouver, British Columbia, Canada
- Children'S Health Research Institute
Brussel, Ontario, Canada
- Mcgill University Health Centre
Montreal, Quebec, Canada
- Armand Trousseau Hospital, I-Motion
Paris, Paris 9, France
- Lmu-Campus Innenstadt
Munich, Bavaria, Germany
- Universitatsklinikum Essen
Essen, Germany
- Universitaetsklinikum Freiburg
Freiburg im Breisgau, Germany
- the University of Hong Kong
Hong Kong, Hong Kong SAR, Hong Kong
- Pediatric Neurology Unit, Catholic University
Essen, Italy
- Istituto Giannina Gaslini, Centro Traslazionale Di Miologia
Genova, Italy
- Department of Neuroscience, Università Di Messina, Aou Polic
Messina, Italy
- Aichi Children'S Health and Medical Center
Ōbu, Aichi-ken, Japan
- Hyogo College of Medicine
Nishinomiya, Hyōgo, Japan
- Tokyo Women'S Medical University
Shinjuku-ku, Tokyo, Japan
- Kumamoto University Hospital
Kumamoto, Japan
- Miyagi Prefectural Children Hospital
Miyagi, Japan
- University of Miyazaki Hospital
Miyazaki, Japan
- Seoul National University Hospital
Seoul, Korea, South Korea
- Hospital Sant Joan de Deu
Barcelona, Spain
- Hospital Universitario Vall de Hebron
Hebron, Spain
- Hospital Universitario la Paz
Madrid, Spain
- the Queen Silvia Children'S Hospital
Gothenburg, Sweden
- Uníversity of Hacettepe
Ankara, Turkey (Türkiye)
- Marmara University Pendik Training and Research Hospital
Istanbul, Turkey (Türkiye)
- Mrc Centre for Neuromuscular Diseases at Newcastle
Newcastle, Northumberland, United Kingdom
- Ucl Institute of Child Health
London, United Kingdom
- David Geffen School of Medicine at Ucla
Los Angeles, California, United States
- Stanford University School of Medicine
Palo Alto, California, United States
- Children'S Hospital Colorado
Aurora, Colorado, United States
- Connecticut Children'S Medical Center
Hartford, Connecticut, United States
- Nemours Children'S Clinic
Orlando, Florida, United States
- Ann & Robert H. Lurie Children'S Hospital of Chicago
New York, Illinois, United States
- the Johns Hopkins Hospital
Baltimore, Maryland, United States
- Boston Children'S Hospital
Boston, Massachusetts, United States
- Gillette Children'S Specialty Healthcare
Saint Paul, Minnesota, United States
- Washington University School of Medicine
St Louis, Missouri, United States
- Columbia University Medical Center
New York, New York, United States
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 4 Nov 2015
- Primary completion
- 21 Aug 2023
- Completion
- 21 Aug 2023
- Last update posted
- 22 Oct 2024
- Registered enrollment
- 292
- Registry id
- NCT02594124
Cross-registrations
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.