The Myelin Disorders Biorepository Project
Summary
The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Adeline Vanderver, MD
Children's Hospital of Philadelphia
Principal Investigator
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
23 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- Children'S Hospital of Los Angeles
Los Angeles, California, United States
Recruiting - Children'S Hospital of Orange County
Orange, California, United States
Recruiting - Stanford University (lucile Packard Children'S Hospital)
Palo Alto, California, United States
Recruiting - University of California, Davis (uc Davis Health)
Sacramento, California, United States
Recruiting - University of California, San Diego (rady Children'S Hospital)
San Diego, California, United States
Recruiting - Ucsf Benioff Children'S Hospital
San Francisco, California, United States
Recruiting - Children'S National Medical Center
Washington D.C., District of Columbia, United States
Recruiting - Emory University (children'S Healthcare of Atlanta)
Atlanta, Georgia, United States
Recruiting - Ann & Robert H. Lurie Children'S Hospital of Chicago
Chicago, Illinois, United States
Recruiting - Kennedy Krieger Institute
Baltimore, Maryland, United States
Recruiting - Massachusetts General Hospital (mgh)
Boston, Massachusetts, United States
Recruiting - University of Minnesota
Minneapolis, Minnesota, United States
Recruiting - Mayo Clinic
Rochester, Minnesota, United States
Recruiting - Atrium Health Wake Forest Baptist
Winston-Salem, North Carolina, United States
Recruiting - Akron Children'S Hospital
Akron, Ohio, United States
Recruiting - Nationwide Children'S Hospital
Columbus, Ohio, United States
Recruiting - the Children'S Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
Adeline Vanderver, MDAmy Waldman, MD, MSCELaura Adang, MD, PhD, MSTRRecruiting - University of Pennsylvania
Philadelphia, Pennsylvania, United States
Recruiting - University of Pittsburgh Medical Center
Pittsburgh, Pennsylvania, United States
Recruiting - Baylor College of Medicine (texas Children'S Hospital)
Houston, Texas, United States
Recruiting - Ut Health Houston
Houston, Texas, United States
Recruiting - University of Utah (primary Children'S Hospital)
Salt Lake City, Utah, United States
Recruiting - Seattle Children'S Hospital
Seattle, Washington, United States
Recruiting
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 8 Dec 2016
- Primary completion
- 8 Dec 2030
- Completion
- 8 Dec 2030
- Last update posted
- 23 Oct 2025
- Registered enrollment
- 12,000
- Registry id
- NCT03047369
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.