findmyKOL
Clinical trialNCT03519711CompletedPhase 1/PHASE2Interventional

A Study of PTC923 (CNSA-001) in Primary Tetrahydrobiopterin (BH4) Deficient Participants With Hyperphenylalaninemia

SponsorPTC TherapeuticsEnrollment8BH4 DeficiencyHyperphenylalaninemia
View the registry record on ClinicalTrials.gov

Summary

The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →

Investigators

The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.

A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.

Sites

4 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.

United States
  • University of Minnesota

    Minneapolis, Minnesota, United States

  • Ut Southwestern

    Dallas, Texas, United States

  • University of Utah Hospital

    Salt Lake City, Utah, United States

  • Marshfield Clinic

    Marshfield, Wisconsin, United States

Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.

Drugs studied

No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →

Registration & key dates

Registry attributes as recorded on the ClinicalTrials.gov study record.

Start
3 Jan 2019
Primary completion
2 Oct 2020
Completion
2 Oct 2020
Last update posted
14 Nov 2023
Registered enrollment
8
Registry id
NCT03519711

Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.