FindMyKOL
Clinical trialNCT03709784Active, not recruitingObservational

Spinraza in Adult Spinal Muscular Atrophy

SponsorWashington University School of MedicineEnrollment148Spinal Muscular AtrophySpinal Muscular Atrophy Type 3Spinal Muscular Atrophy Type II
View the registry record on ClinicalTrials.gov

Summary

The lay summary the sponsor registered on ClinicalTrials.gov.

This is a longitudinal, observational study of adult patients with genetically confirmed chromosome 5q SMA to examine the safety, tolerability, and effectiveness of SPINRAZA® (nusinersen) for up to 30 months.
clinicaltrials.gov ↗

Investigators

The overall officials registered on this study. Names that resolve to a FindMyKOL profile link to it; the rest are shown as registered.

A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.

Sites

11 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.

Canada
  • Montreal Neurological Institute and Hospital

    Montreal, Quebec, Canada

United States
  • Barrow Neurological Institute

    Phoenix, Arizona, United States

  • Georgetown University

    Washington D.C., District of Columbia, United States

  • Johns Hopkins

    Baltimore, Maryland, United States

  • Massachusetts General Hospital-Harvard University

    Boston, Massachusetts, United States

  • Memorial Healthcare

    Owosso, Michigan, United States

  • Washington University School of Medicine

    St Louis, Missouri, United States

  • New York University School of Medicine

    New York, New York, United States

  • Houston Methodist Neurological Institute

    Houston, Texas, United States

  • Children'S Hospital of the King'S Daughthers

    Norfolk, Virginia, United States

  • University of Washington

    Seattle, Washington, United States

Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.

Drugs studied

The drug and biological interventions registered on this study, normalized to their RxNorm ingredient where possible.

Observational study to examine safety, tolerability, and effectiveness of SPINRAZA® prescribed as part of standard of care
Linked drugs open the directory filtered to KOLs working with them.clinicaltrials.gov ↗

Registration & key dates

Registry attributes as recorded on the ClinicalTrials.gov study record.

Start
16 Aug 2018
Primary completion
31 Dec 2024
Completion
1 Jan 2025
Last update posted
20 Nov 2024
Registered enrollment
148
Registry id
NCT03709784
clinicaltrials.gov ↗

Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 4 Nov 2026. Registry facts are shown as registered by the study sponsor; FindMyKOL does not interpret them.