findmyKOL
Clinical trialNCT03952156TerminatedPhase 1/PHASE2Interventional

Gene Therapy Clinical Study in Adult PKU

SponsorHomology Medicines, IncEnrollment10PAH DeficiencyPhenylketonurias
View the registry record on ClinicalTrials.gov

Summary

The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →

Investigators

The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.

A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.

Sites

13 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.

United States
  • Kaiser Permanente Los Angeles Medical Center

    Los Angeles, California, United States

  • Children'S Hospital of Orange County

    Orange, California, United States

  • University of South Florida

    Tampa, Florida, United States

  • Emory University Hospital

    Atlanta, Georgia, United States

  • Lurie Children'S Hospital of Chicago

    Chicago, Illinois, United States

  • Boston Children'S Hospital

    Boston, Massachusetts, United States

  • Icahn School of Medicine at Mount Sinai

    New York, New York, United States

  • the University of North Carolina at Chapel Hill

    Chapel Hill, North Carolina, United States

  • Nationwide Children'S Hospital

    Columbus, Ohio, United States

  • Children'S Hospital of Philadelphia

    Philadelphia, Pennsylvania, United States

  • Upmc Children'S Hospital of Pittsburgh

    Pittsburgh, Pennsylvania, United States

  • University of Texas Southwestern Medical Center

    Dallas, Texas, United States

  • University of Utah

    Salt Lake City, Utah, United States

Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.

Drugs studied

No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →

Registration & key dates

Registry attributes as recorded on the ClinicalTrials.gov study record.

Start
10 Jun 2019
Primary completion
10 Jan 2023
Completion
1 Aug 2023
Last update posted
29 Aug 2023
Registered enrollment
10
Registry id
NCT03952156

Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.