Multi-Center Study of ManNAc for GNE Myopathy
Summary
The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Anthony A. Amato, MD
Brigham and Women's Hospital
Principal Investigator - Francis Rossignol, MD
National Institutes of Health (NIH)
Principal Investigator
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
10 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- Ucla
Los Angeles, California, United States
- University of Iowa
Iowa City, Iowa, United States
- University of Kansas, Medical Center
Kansas City, Kansas, United States
- Nih Clinical Center
Bethesda, Maryland, United States
- Brigham and Women'S Hospital
Boston, Massachusetts, United States
- Washington University
St Louis, Missouri, United States
- Columbia University Medical Center
New York, New York, United States
- University of Rochester
Rochester, New York, United States
- Ohio State University, Wexner Medical Center
Columbus, Ohio, United States
- University of Utah
Salt Lake City, Utah, United States
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 5 Apr 2022
- Primary completion
- 27 Jun 2025
- Completion
- 30 Oct 2025
- Last update posted
- 13 Jun 2025
- Registered enrollment
- 54
- Registry id
- NCT04231266
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.