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Clinical trialNCT04509050RecruitingObservational

Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children

SponsorSonya HeltsheEnrollment210Cystic Fibrosis
View the registry record on ClinicalTrials.gov

Summary

The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →

Investigators

The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.

A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.

Sites

35 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.

United States
  • the Children'S Hospital Alabama, University of Alabama at Birmingham

    Birmingham, Alabama, United States

    Recruiting
  • Stanford University Medical Center

    Palo Alto, California, United States

    Recruiting
  • Children'S Hospital Colorado

    Aurora, Colorado, United States

    Recruiting
  • Nemours Children'S Clinic

    Jacksonville, Florida, United States

    Recruiting
  • University of Miami

    Miami, Florida, United States

    Recruiting
  • the Nemours Children'S Clinic - Orlando

    Orlando, Florida, United States

    Recruiting
  • Riley Hospital for Children

    Indianapolis, Indiana, United States

    Recruiting
  • University of Iowa

    Iowa City, Iowa, United States

    Recruiting
  • University of Kansas Medical Center

    Kansas City, Kansas, United States

    Recruiting
  • Boston Children'S Hospital

    Boston, Massachusetts, United States

    Recruiting
  • University of Michigan, Michigan Medicine

    Ann Arbor, Michigan, United States

    Recruiting
  • Helen Devos Children'S Hospital

    Grand Rapids, Michigan, United States

    Recruiting
  • Children'S Hospitals and Clinics of Minnesota

    Minneapolis, Minnesota, United States

    Recruiting
  • the Minnesota Cystic Fibrosis Center

    Minneapolis, Minnesota, United States

    Recruiting
  • Children'S Mercy Kansas City

    Kansas City, Missouri, United States

    Recruiting
  • St. Louis Children'S Hospital

    St Louis, Missouri, United States

    Recruiting
  • the Cystic Fibrosis Center of Western New York

    Buffalo, New York, United States

    Recruiting
  • Children'S Hospital of New York

    New York, New York, United States

    Recruiting
  • Suny Upstate Medical University

    Syracuse, New York, United States

    Recruiting
  • New York Medical College at Westchester Medical Center

    Valhalla, New York, United States

    Recruiting
  • Cincinnati Children'S Hospital Medical Center

    Cincinnati, Ohio, United States

    Recruiting
  • Nationwide Children'S Hospital

    Columbus, Ohio, United States

    Recruiting
  • Oklahoma Cystic Fibrosis Center

    Oklahoma City, Oklahoma, United States

    Recruiting
  • Oregon Health Sciences University

    Portland, Oregon, United States

    Recruiting
  • Hershey Medical Center Pennsylvania State University

    Hershey, Pennsylvania, United States

    Recruiting
  • Children'S Hospital of Philadelphia

    Philadelphia, Pennsylvania, United States

    Recruiting
  • Children'S Hospital of Pittsburgh of Upmc

    Pittsburgh, Pennsylvania, United States

    Recruiting
  • University of Texas Southwestern / Children'S Health

    Dallas, Texas, United States

    Recruiting
  • Cook Children'S Medical Center

    Fort Worth, Texas, United States

    Recruiting
  • Baylor College of Medicine

    Houston, Texas, United States

    Recruiting
  • Primary Children'S Cystic Fibrosis Center

    Salt Lake City, Utah, United States

    Recruiting
  • Vermont Children'S Hospital

    Burlington, Vermont, United States

    Recruiting
  • University of Virginia

    Charlottesville, Virginia, United States

    Recruiting
  • Seattle Children'S Hospital

    Seattle, Washington, United States

    Recruiting
  • University of Wisconsin

    Madison, Wisconsin, United States

    Recruiting

Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.

Drugs studied

No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →

Registration & key dates

Registry attributes as recorded on the ClinicalTrials.gov study record.

Start
18 Nov 2020
Primary completion
31 Dec 2027
Completion
31 Dec 2027
Last update posted
8 Jul 2026
Registered enrollment
210
Registry id
NCT04509050

Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.