Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children
Summary
The lay summary the sponsor registered on ClinicalTrials.gov.
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Katie Larson Ode, MD
University of Iowa
Principal Investigator - Lucas Hoffman, MD PhD
University of Washington/Seattle Children's
Principal Investigator
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
35 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- the Children'S Hospital Alabama, University of Alabama at Birmingham
Birmingham, Alabama, United States
Recruiting - Stanford University Medical Center
Palo Alto, California, United States
Recruiting - Children'S Hospital Colorado
Aurora, Colorado, United States
Recruiting - Nemours Children'S Clinic
Jacksonville, Florida, United States
Recruiting - University of Miami
Miami, Florida, United States
Recruiting - the Nemours Children'S Clinic - Orlando
Orlando, Florida, United States
Recruiting - Riley Hospital for Children
Indianapolis, Indiana, United States
Recruiting - University of Iowa
Iowa City, Iowa, United States
Recruiting - University of Kansas Medical Center
Kansas City, Kansas, United States
Recruiting - Boston Children'S Hospital
Boston, Massachusetts, United States
Recruiting - University of Michigan, Michigan Medicine
Ann Arbor, Michigan, United States
Recruiting - Helen Devos Children'S Hospital
Grand Rapids, Michigan, United States
Recruiting - Children'S Hospitals and Clinics of Minnesota
Minneapolis, Minnesota, United States
Recruiting - the Minnesota Cystic Fibrosis Center
Minneapolis, Minnesota, United States
Recruiting - Children'S Mercy Kansas City
Kansas City, Missouri, United States
Recruiting - St. Louis Children'S Hospital
St Louis, Missouri, United States
Recruiting - the Cystic Fibrosis Center of Western New York
Buffalo, New York, United States
Recruiting - Children'S Hospital of New York
New York, New York, United States
Recruiting - Suny Upstate Medical University
Syracuse, New York, United States
Recruiting - New York Medical College at Westchester Medical Center
Valhalla, New York, United States
Recruiting - Cincinnati Children'S Hospital Medical Center
Cincinnati, Ohio, United States
Recruiting - Nationwide Children'S Hospital
Columbus, Ohio, United States
Recruiting - Oklahoma Cystic Fibrosis Center
Oklahoma City, Oklahoma, United States
Recruiting - Oregon Health Sciences University
Portland, Oregon, United States
Recruiting - Hershey Medical Center Pennsylvania State University
Hershey, Pennsylvania, United States
Recruiting - Children'S Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
Recruiting - Children'S Hospital of Pittsburgh of Upmc
Pittsburgh, Pennsylvania, United States
Recruiting - University of Texas Southwestern / Children'S Health
Dallas, Texas, United States
Recruiting - Cook Children'S Medical Center
Fort Worth, Texas, United States
Recruiting - Baylor College of Medicine
Houston, Texas, United States
Recruiting - Primary Children'S Cystic Fibrosis Center
Salt Lake City, Utah, United States
Recruiting - Vermont Children'S Hospital
Burlington, Vermont, United States
Recruiting - University of Virginia
Charlottesville, Virginia, United States
Recruiting - Seattle Children'S Hospital
Seattle, Washington, United States
Recruiting - University of Wisconsin
Madison, Wisconsin, United States
Recruiting
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
The drug and biological interventions registered on this study, normalized to their RxNorm ingredient where possible.
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 18 Nov 2020
- Primary completion
- 31 Dec 2027
- Completion
- 31 Dec 2027
- Last update posted
- 8 Jul 2026
- Registered enrollment
- 210
- Registry id
- NCT04509050
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 24 Aug 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.