Gene Correction in Autologous CD34+ Hematopoietic Stem Cells (HbS to HbA) to Treat Severe Sickle Cell Disease
Summary
The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Matthew Porteus, MD, PhD
Kamau Therapeutics
Study Director
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
6 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- Children'S Hospital Los Angeles
Los Angeles, California, United States
Ashley Gray, MDRecruiting - Lucile Packard Children'S Hospital
Palo Alto, California, United States
David Shyr, MDMay Chien, MDRecruiting - Washington University
St Louis, Missouri, United States
John F Dipersio, MD, PhDRecruiting - Columbia University Irving Medical Center
New York, New York, United States
Marcus Mapara, MDMonica Bhatia, MDRecruiting - Memorial Sloan Kettering
New York, New York, United States
Jaap Jan Boelens, MD, PhDRecruiting - Nationwide Children'S Hospital
Columbus, Ohio, United States
Recruiting
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 15 Nov 2021
- Primary completion
- 31 Dec 2026
- Completion
- 31 Dec 2028
- Last update posted
- 2 Jul 2026
- Registered enrollment
- 15
- Registry id
- NCT04819841
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.