A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy
Summary
The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Lindsey Lair, MD
Biohaven Pharmaceuticals, Inc.
Study Director
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
53 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- University Hospital Antwerp
Edegem, Belgium
- University Hospital Ghent
Ghent, Belgium
- University Hospital Leuven
Leuven, Belgium
- University Hospital Brno - Dept. of Pediatric Neurology
Brno, Czechia
- Motol University Hospital
Prague, Czechia
- University Hospital Essen (public-Law Institution) - Dept. of Pediatrics I
Essen, Germany
- University Hospital Freiburg, Center for Children and Adolescent Medicine, Dept. of Neuropediatrics and Muscle Disorders
Freiburg im Breisgau, Germany
- Dr. Von Haunersches Children'S Hospital - Lmu Munich
Munich, Germany
- Irccs Institute of Neurological Sciences of Bologna - Bellaria Hospital
Bologna, Italy
- Nemo-Brescia Clinical Center for Neuromuscular Diseases
Gussago, Italy
- Irccs Neurological Institute C. Mondino Child and Neuropsychiatric Unit
Pavia, Italy
- Bambino Gesù Children'S Research Hospital Irccs - San Paolo Office Dept. of Neuroscience
Roma, Italy
- University Medical Center Utrecht
Utrecht, Netherlands
- University Clinical Centre in Gdansk - Dept. of Developmental Neurology
Gdansk, Poland
- Heliodor Swiecicki Clinical Hospital at Medical University - Child and Adolescents Neurology Clinic
Poznan, Poland
- the Children'S Memorial Health Institute - Dept. of Neurology and Epileptology
Warsaw, Poland
- T. Marciniak Lower Silesian Specialist Hospital, Pediatric Neurology Dept.
Wroclaw, Poland
- Donostia University Hospital
Donostia / San Sebastian, Spain
- Hospital Sant Joan de Déu
Esplugues de Llobregat, Spain
- Maternal-Child'S Hospital of Málaga, Regional University Hospital - Pediatric Neurology Unit
Málaga, Spain
- la Fe University and Polytechnic Hospital
Valencia, Spain
- Royal Hospital for Children
Glasgow, Scotland, United Kingdom
- John Radcliffe Hospital
Oxford, United Kingdom
- Phoenix Children'S
Phoenix, Arizona, United States
- Ucsd & Rady Children'S
La Jolla, California, United States
- Children'S Hospital of Los Angeles
Los Angeles, California, United States
- Ucsf Benioff Children'S Hospital, Medical Center
San Francisco, California, United States
- Children'S Hospital Colorado
Aurora, Colorado, United States
- Uf Health, Shands Hospital
Gainesville, Florida, United States
- Rare Disease Research
Atlanta, Georgia, United States
- Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children'S Hospital of Chicago
Chicago, Illinois, United States
- Indiana University -Riley Research
Indianapolis, Indiana, United States
- University of Iowa
Iowa City, Iowa, United States
- University of Kansas Medical Center
Fairway, Kansas, United States
- Boston Children'S Hospital - Harvard
Boston, Massachusetts, United States
- Bshs Office of Research
Grand Rapids, Michigan, United States
- Washington University in St. Louis
St Louis, Missouri, United States
- Columbia University Medical Center
New York, New York, United States
- Stony Brook University Hospital
Stony Brook, New York, United States
- Duke University Medicine
Durham, North Carolina, United States
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 6 Jul 2022
- Primary completion
- 25 Sept 2024
- Completion
- 31 Dec 2027
- Last update posted
- 1 Jun 2026
- Registered enrollment
- 269
- Registry id
- NCT05337553
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.