A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II)
Summary
The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Jose Alcantara Rodriguez, PharmD
Denali Therapeutics Inc.
Study Director
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
32 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- Sanatorio Mater Dei
Buenos Aires, Argentina
Alejandro Fainboim, MDRecruiting
- Women'S and Children'S Hospital
North Adelaide, Australia
Withdrawn
- Uz Antwerpen
Antwerp, Antwerpen, Belgium
Francois Eyskens, MDRecruiting - Universitair Ziekenhuis Brussel
Jette, Brussels Capital, Belgium
Luc Regal, MDRecruiting
- Hospital de Clínicas de Porto Alegre (hcpa) - Ppds
Porto Alegre, Brazil
Carolina Fischinger Moura de Souza, MDRecruiting - Instituto Fernandes Figueira
Rio de Janeiro, Brazil
Withdrawn
- University of Alberta - Faculty of Medicine & Dentistry
Edmonton, Alberta, Canada
Saadet Andrews, MDRecruiting - Hospital for Sick Children
Toronto, Ontario, Canada
Michal Inbar-Feigenberg, MDRecruiting - Mcgill University Health Center
Montreal, Quebec, Canada
John Mitchell, MDRecruiting
- Vseobecna Fakultni Nemocnice V Praze
Prague, Czechia
Martin Magner, MDRecruiting
- Hôpital Jeanne de Flandre
Lille, France
Anne-Sophie Guémann, MDRecruiting
- Sphincs
Höchheim, Hochheim, Germany
Eugen Mengel, MDRecruiting - Medizinische Universität Lausitz - Carl Thiem
Cottbus, Germany
Simone Stolz, MDRecruiting
- Azienda Sanitaria Universitaria Friuli Centrale - Po Universitario Santa Maria Della Misericordia
Udine, Italy
Maurizio Scarpa, MDRecruiting
- Erasmus Medical Center - Sophia Children'S Hospital
Rotterdam, Rotterdam, Netherlands
Hannerieke van den Hout, MDRecruiting
- Hospital Universitario Vall D'Hebron
Barcelona, Barcelona, Spain
Mireia del Toro, MDRecruiting - Hospital Infantil Universitario Niño Jesus
Madrid, Madrid, Spain
Laura Lopez Marin, MDRecruiting
- Drottning Silvias Barn Och Ungdomssjukhus
Gothenburg, Sweden
Niklas Darin, MD, PhDRecruiting
- Cukurova University Medical Faculty Balcali Hospital
Adana, Turkey (Türkiye)
Neslihan Mungan, MDRecruiting - Gazi Universitesi Tip Fakultesi
Çankaya, Turkey (Türkiye)
Fatih Suheyl Ezgu, MDRecruiting
- Great Ormond Street Hospital for Children
London, London, United Kingdom
Spyros Batzios, MDRecruiting - Birmingham Women'S and Children'S Nhs Foundation Trust
Birmingham, United Kingdom
Julian Raiman, MDRecruiting - Royal Free Hospital
London, United Kingdom
Uma Ramaswami, MDRecruiting - Salford Royal Hospital
Salford, United Kingdom
Karolina Stepien, MDRecruiting
- Ucsf Benioff Children'S Hospital Oakland
Oakland, California, United States
Paul Harmatz, MDRecruiting - Ann and Robert H Lurie Children'S Hospital of Chicago
Chicago, Illinois, United States
Barbara Burton, MDRecruiting - Hackensack University Medical Center
Hackensack, New Jersey, United States
Helio Pedro, MDRecruiting - Unc Children'S Research Institute
Chapel Hill, North Carolina, United States
Joseph Muenzer, MDRecruiting - Cincinnati Children'S Hospital Medical Center
Cincinnati, Ohio, United States
Nancy Leslie, MDRecruiting - Children'S Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
Can Ficicioglu, MDRecruiting - the University of Texas Medical School at Houston
Houston, Texas, United States
Paul Hillman, MDRecruiting - University of Utah, Ppds
Salt Lake City, Utah, United States
David Viskochil, MDRecruiting
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 21 Jul 2022
- Primary completion
- 31 Dec 2027
- Completion
- 31 Dec 2027
- Last update posted
- 5 Aug 2025
- Registered enrollment
- 63
- Registry id
- NCT05371613
Cross-registrations
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.