Tovorafenib for Treatment of Craniopharyngioma in Children and Young Adults
Summary
The lay summary the sponsor registered on ClinicalTrials.gov.
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Cassie Kline, MD
Children's Hospital of Philadelphia
Study Chair - Sabine Mueller, MD, PhD, MAS
University of California, San Francisco
Principal Investigator
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
20 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- John Hunter Children'S Hospital
New Lambton Heights, New South Wales, Australia
Frank Alvaro, MMBS, FRACPRecruiting - Royal Hobart Hospital
Hobart, Tasmania, Australia
Tom Walwyn, A/ProfRecruiting - Children'S Cancer Centre, Monash Children'S Hospital
Clayton, VIC 3168, Australia
Peter Downie, A/ProfRecruiting - Royal Children'S Hospital, Childrens' Cancer Centre
Parkville, Victoria, Australia
Dong Anh Khuong Quang, MD, MSc, PhD, FRACPRecruiting - Perth Children'S Hospital
Nedlands, Western Australia, Australia
Santosh ValviRecruiting
- University of Alabama at Birmingham
Birmingham, Alabama, United States
Girish Dhall, MDRecruiting - Rady Children'S Hospital/university of California, San Diego
San Diego, California, United States
Jennifer Elster, MDRecruiting - University of California, San Francisco
San Francisco, California, United States
Sabine Mueller, MD, PhD, MASRecruiting - University of Florida
Gainesville, Florida, United States
Elias Sayour, MD, PhDRecruiting - Ann & Robert H. Lurie Children'S Hospital of Chicago
Chicago, Illinois, United States
Ashley Plant-Fox, MDRecruiting - Riley Hospital for Children at Indiana University Health
Indianapolis, Indiana, United States
Scott Coven, MDRecruiting - John Hopkins University
Baltimore, Maryland, United States
Kenneth Cohen, MD, MBARecruiting - Dana-Farber/boston Children'S Harvard Medical School
Boston, Massachusetts, United States
Susan Chi, MDRecruiting - University of Michigan
Ann Arbor, Michigan, United States
Andrea Franson, MDRecruiting - Children'S Minnesota
Minneapolis, Minnesota, United States
Anne Bendel, MDMaggie Skrypek, MDRecruiting - St. Louis Children'S Hospital Washington University
St Louis, Missouri, United States
Mohamed Shebl Abdelbaki, MDRecruiting - Nyu Langone Health
New York, New York, United States
Jessica Clymer, MDRecruiting - Duke University Medical Center
Durham, North Carolina, United States
Daniel Landi, MDRecruiting - Children'S Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
Cassie Kline, MD, MASRecruiting - University of Utah
Salt Lake City, Utah, United States
Nicholas Whipple, MD, MPHRecruiting
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
The drug and biological interventions registered on this study, normalized to their RxNorm ingredient where possible.
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 12 Sept 2022
- Primary completion
- 1 Mar 2027
- Completion
- 1 Mar 2028
- Last update posted
- 23 Apr 2026
- Registered enrollment
- 57
- Registry id
- NCT05465174
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 24 Aug 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.