Clinical trialNCT06214507RecruitingObservational

Danon Disease Natural History Study

SponsorRocket Pharmaceuticals Inc.Enrollment60Danon Disease

View the registry record on ClinicalTrials.gov

Summary

The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →

Investigators

No overall officials are registered on this study record. Site-level investigators, where published, appear with their sites below. Why? →

A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.

Sites

13 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.

Germany

German Heart Center Munich
München, Germany
Cordula Wolf, MD
Recruiting

Israel

Sheba Medical Center
Ramat Gan, Israel
Yair Anikster, MD
Recruiting

Italy

Azienda Ospedaliera Universitaria Meyer Irccs
Florence, Italy
Iacopo Olivotto, MD
Recruiting

Spain

Hospital Universitario Puerta de Hierro Majadahonda
Majadahonda, Madrid, Spain
Pavia Garcia, MD
Recruiting

United Kingdom

University College London - Great Ormond Street Institute of Child Health
London, United Kingdom
Juan Kaski, MDZhia Lim, MD
Recruiting

United States

Phoenix Children'S Hospital
Phoenix, Arizona, United States
Andrew Papez, MD
Recruiting
University of California, San Diego
La Jolla, California, United States
Kimberly Hong, MD
Recruiting
Children'S Hospital Colorado
Aurora, Colorado, United States
Matthew Taylor, MD
Recruiting
University of Florida College of Medicine
Gainesville, Florida, United States
Mohammed M Ahmed, MD
Recruiting
University of Michigan
Ann Arbor, Michigan, United States
Josh Meisner, MDSupriya Shore, MD
Recruiting
Washington University
St Louis, Missouri, United States
Charles Canter, MD
Recruiting
Columbia University Medical Center/new York Presbyterian
New York, New York, United States
Farhana Latif, MD
Recruiting
Texas Children'S Hospital
Houston, Texas, United States
Kyle Hope, MD
Recruiting

Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.

Drugs studied

No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →

Registration & key dates

Registry attributes as recorded on the ClinicalTrials.gov study record.

Start: 20 Dec 2023
Primary completion: 31 Dec 2029
Completion: 31 Mar 2030
Last update posted: 5 May 2026
Registered enrollment: 60
Registry id: NCT06214507

clinicaltrials.gov ↗

Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.