findmyKOL
Clinical trialNCT06747884RecruitingObservational

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

SponsorVirginia Commonwealth UniversityEnrollment200Childhood Myotonic DystrophyCongenital Myotonic DystrophyMyotonic Dystrophy
View the registry record on ClinicalTrials.gov

Summary

The lay summary the sponsor registered on ClinicalTrials.gov.

This is a natural history study to improve the types of assessments and biological samples that will be used in clinical drug trials in both congenital myotonic dystrophy and childhood myotonic dystrophy.
clinicaltrials.gov ↗

Investigators

The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.

A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.

Sites

4 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.

Brazil
  • Hospital Das Clínicas, University of São Paulo School of Medicine (hcfmusp)

    Cerqueira César, São Paulo, Brazil

    Clara Gontijo Camelo, MD, PhD
    Not, yet, recruiting
United States
  • Arkansas Children'S Hospital

    Little Rock, Arkansas, United States

    Aravindhan Veerapandiyan, MD
    Not, yet, recruiting
  • University of Kansas Medical Center

    Kansas City, Kansas, United States

    Jeffrey Statland, MD
    Not, yet, recruiting
  • Virginia Commonwealth University

    Richmond, Virginia, United States

    Nicholas E Johnson, MD, MSCI, FAAN
    Recruiting

Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.

Drugs studied

No drug or biological interventions are in our data for this study. It may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →

Registration & key dates

Registry attributes as recorded on the ClinicalTrials.gov study record.

Start
6 Jun 2025
Primary completion
30 Jun 2030
Completion
30 Jun 2030
Last update posted
11 Aug 2026
Registered enrollment
200
Registry id
NCT06747884
clinicaltrials.gov ↗

Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 24 Aug 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.