Efficacy and Safety Study of Genetically Targeted Enzyme Replacement Therapy for Advanced Heart Failure
Summary
The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- A. G. Kfoury, MD
Intermountain Health Care, Inc.
Principal Investigator - Andrew Kao, MD
Mid America Heart Institute, Saint Luke's Hospital
Principal Investigator - Barry Greenberg, MD
University of California at San Diego Medical Center
Principal InvestigatorKOL profile → - Barry London, MD
University of Pittsburgh Medical Center
Principal Investigator - Brian Jaski, MD
San Diego Cardiac Center
Principal Investigator - Daniel Pauly, MD
Shands Hospital, University of Florida at Gainesville
Principal Investigator - Dinesh K. Gupta, MD
Tennessee Center for Clinical Trials, Harton Regional Medical Center
Principal Investigator - Donna Mancini, MD
Columbia University Hospital
Principal Investigator - Douglas W. Losordo, MD
Northwestern University
Principal Investigator - Eric J. Eichhorn, MD, FACC
Cardiopulmonary Research Science and Technology Institutte, Medical City Dallas Hospital
Principal Investigator - Guillermo Torre, MD
The Methodist Hospital Research Institute
Principal Investigator - Jill Kalman, MD
Icahn School of Medicine at Mount Sinai
Principal Investigator - Joaquin E. Cigarroa, MD
Oregon Health and Science University
Principal Investigator - Marc Klapholz, MD
University of Medicine and Dentistry of New Jersey
Principal Investigator - Mariell Jessup, MD
University of Pennsylvania
Study Chair - Mark Dunlap, MD
MetroHealth Medical Center
Principal Investigator - Maryl R. Johnson, MD
University of Wisconsin, Madison
Principal Investigator - Paul J. Hauptman, MD
St. Louis University Hospital
Principal Investigator - Randall Starling, MD
The Cleveland Clinic
Principal Investigator - Stephanie H. Dunlap, DO
University of Cincinnati
Principal Investigator - Stephen Archer, MD
University of Chicago
Principal Investigator - Vinay Thohan, MD
Wake Forest University
Principal Investigator
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
22 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- San Diego Cardiac Center
San Diego, California, United States
- University of California at San Diego Medical Center
San Diego, California, United States
- Shands Hospital at University of Florida
Gainesville, Florida, United States
- Northwestern University
Chicago, Illinois, United States
- University of Chicago Medical Center
Chicago, Illinois, United States
- Mid America Heart Institute, Saint Luke'S Hospital
Kansas City, Missouri, United States
- St. Louis University Hospital
St Louis, Missouri, United States
- University of Medicine and Dentistry of New Jersey
Newark, New Jersey, United States
- Columbia University Hospital
New York, New York, United States
- Mount Sinai Medical Center
New York, New York, United States
- Wake Forest University
Winston-Salem, North Carolina, United States
- University of Cincinnati
Cincinnati, Ohio, United States
- Cleveland Clinic Foundation
Cleveland, Ohio, United States
- Metrohealth Medical Center
Cleveland, Ohio, United States
- Oregon Health and Science University
Portland, Oregon, United States
- Hospital of the University of Pennsylvania
Philadelphia, Pennsylvania, United States
- University of Pittsburgh Medical Center, Presbyterian-Shadyside Hospital
Pittsburgh, Pennsylvania, United States
- Tennessee Center for Clinical Trials & Harton Regional Medical Center
Tullahoma, Tennessee, United States
- Cardiopulmonary Research Science and Technology Institute, Medical City Dallas Hospital
Dallas, Texas, United States
- Methodist Hospital
Houston, Texas, United States
- Intermountain Medical Center
Murray, Utah, United States
- University of Wisconsin
Madison, Wisconsin, United States
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 31 Mar 2007
- Primary completion
- 31 Aug 2010
- Completion
- 31 Aug 2012
- Last update posted
- 20 Aug 2014
- Registered enrollment
- 51
- Registry id
- NCT00454818
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.