A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
Summary
The lay summary the sponsor registered on ClinicalTrials.gov.
Investigators
The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.
- Joseph Rossano, MD
Children's Hospital of Philadelphia
Principal Investigator
A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.
Sites
6 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.
- German Heart Center Munich
Munich, Germany
Recruiting
- Meyer Childrens Hospital
Florence, Italy
Recruiting
- Great Ormund Street Hospital & Ucl Institute of Cardiovascular Science
London, United Kingdom
Recruiting
- University of California, San Diego
La Jolla, California, United States
Recruiting - Boston Children'S Hospital
Boston, Massachusetts, United States
Dominic Abrams, MDRecruiting - Children'S Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
Recruiting
Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.
Drugs studied
No drug or biological interventions are in our data for this study. It may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →
Registration & key dates
Registry attributes as recorded on the ClinicalTrials.gov study record.
- Start
- 5 Sept 2023
- Primary completion
- 30 Apr 2028
- Completion
- 30 Apr 2032
- Last update posted
- 4 May 2026
- Registered enrollment
- 14
- Registry id
- NCT06092034
Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 24 Aug 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.