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Clinical trialNCT05677971RecruitingPhase 3Interventional

Study to Check the Safety of Fazirsiran and Learn if Fazirsiran Can Help People With Liver Disease and Scarring (Fibrosis) Due to an Abnormal Version of Alpha-1 Antitrypsin Protein

SponsorTakedaEnrollment160Alpha1-Antitrypsin Deficiency
View the registry record on ClinicalTrials.gov

Summary

The registered summary isn't in our current data snapshot. Read it on the ClinicalTrials.gov record ↗. Why? →

Investigators

The overall officials registered on this study. Names that resolve to a findmyKOL profile link to it; the rest are shown as registered.

A profile link is shown only when the registered name resolves to a person record with a confident, namesake-checked match; ambiguous names stay unlinked.

Sites

89 registered facilities, with the per-site recruitment status where the registry publishes one. ClinicalTrials.gov does not publish per-site enrollment counts.

Australia
  • Royal Adelaide Hospital

    Adelaide, South Australia, Australia

    Withdrawn
  • St Vincents Hospital Melbourne - Ppds

    Fitzroy, Victoria, Australia

    Matthew Conron
    Recruiting
Austria
  • Lkh-Universitätsklinikum Graz

    Graz, Austria

    Martin Wagner
    Recruiting
  • Medizinische Universität Innsbruck

    Innsbruck, Austria

    Heinz Zoller
    Recruiting
  • Klinikum Klagenfurt Am Wörthersee

    Klagenfurt, Austria

    Markus Peck-Radosavljevic
    Recruiting
  • Medizinische Universität Wien (medical University of Vienna)

    Vienna, Austria

    Mattias Mandorfer
    Recruiting
Belgium
  • Uz Antwerpen

    Antwerp, Belgium

    Sven Francque
    Recruiting
  • Uz Leuven

    Leuven, Belgium

    Jef Verbeek
    Recruiting
Brazil
  • Hospital de Base Do Distrito Federal

    Brasília, Brazil

    Liliana Mendes Sampaio Costa
    Recruiting
  • Hospital Sirio-Libanes

    São Paulo, Brazil

    Gilda Porta
    Recruiting
  • Universidade Estadual Paulista Julio de Mesquita Filho Faculdade de Medicina Campus de Botucatu

    São Paulo, Brazil

    Fernando Romeiro Gomes
    Recruiting
Canada
  • Gi Research Institute

    Vancouver, British Columbia, Canada

    Hin Hin Ko
    Recruiting
  • Queen Elizabeth Ii Health Sciences Center

    Halifax, Nova Scotia, Canada

    Julie Zhu
    Recruiting
  • Inspiration Research Limited

    Toronto, Ontario, Canada

    Kenneth Chapman
    Recruiting
Czechia
  • Institut Klinicke A Experimentalni Mediciny

    Prague, Czechia

    Jan Sperl
    Recruiting
Denmark
  • Hvidovre Hospital

    Hvidovre, Denmark

    Elias Rashu
    Recruiting
France
  • Hôpital Beaujon

    Clichy, France

    Kathleen Milord
    Recruiting
  • Hôpital de la Croix Rousse

    Lyon, France

    Teresa Antonini
    Recruiting
  • Centre Francois Magendie

    Pessac, France

    Maeva Zysman
    Recruiting
  • Hopital Pontchaillou Chu de Rennes

    Rennes, France

    Edouard Bardou-Jacquet
    Recruiting
  • Hospital Purpan

    Toulouse, France

    Lauren Alric
    Recruiting
  • Hôpital Paul Brousse

    Val-de-Marne, France

    Audrey Coilly
    Recruiting
Germany
  • Universitätsklinikum Der Rwth Aachen

    Aachen, Germany

    Pavel Strnad
    Recruiting
  • Charité - Campus Virchow-Klinikum-Ostring 1

    Berlin, Germany

    Frank Tacke
    Recruiting
  • Hannover Medical School

    Hanover, Germany

    Heiner Wedemeyer
    Recruiting
  • Universitätsklinikum Schleswig-Holstein - Campus Kiel

    Kiel, Germany

    Rainer Günther
    Recruiting
  • Universitätsklinikum Tübingen

    Tübingen, Germany

    Christoph Berg
    Recruiting
Ireland
  • Beaumont Hospital

    Dublin, Ireland

    Noel McElvaney
    Recruiting
Italy
  • Fondazione Irccs Cà Granda Ospedale Maggiore Policlinico

    Milan, Italy

    Luca Valenti
    Recruiting
  • Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone

    Palermo, Italy

    Vincenza Calvaruso
    Recruiting
  • Fondazione Irccs Policlinico San Matteo Di Pavia

    Pavia, Italy

    Angelo Corsico
    Recruiting
  • Irccs Istituto Clinico Humanitas

    Rozzano, Italy

    Alessio Aghemo
    Recruiting
Netherlands
  • Amsterdam Umc - Vumc - de Boelelaan

    Amsterdam, Netherlands

    Withdrawn
  • Leiden University Medical Center

    Leiden, Netherlands

    Emily F.A. van 't Wout
    Recruiting
Poland
  • Wip Warsaw Ibd Point Profesor Kierkus

    Warsaw, Poland

    Jaroslaw Kierkus
    Recruiting
  • Id Clinic Arkadiusz Pisula

    Śląskie, Poland

    Withdrawn
Portugal
  • Cca Hospital Braga

    Braga, Portugal

    Carla Rolanda
    Recruiting
  • Hospital Nélio Mendonça

    Funchal, Portugal

    Vitor Pereira
    Recruiting
  • Centro Hospitalar Do Porto

    Porto, Portugal

    Luis Maia
    Recruiting
Spain
  • Hospital Universitario Vall D'Hebron - Ppds

    Barcelona, Spain

    Monica Pons Delgado
    Recruiting
49 more sites on the registry record.ClinicalTrials.gov ↗

Site investigator names are published by ClinicalTrials.gov only while a study recruits, so completed studies list sites without them.

Drugs studied

No drug or biological interventions are in our data for this study — it may test a procedure, device or behavioral intervention, or the intervention list isn't in our current snapshot. See the registry record ↗. Why? →

Registration & key dates

Registry attributes as recorded on the ClinicalTrials.gov study record.

Start
6 Mar 2023
Primary completion
17 Jan 2029
Completion
12 Dec 2031
Last update posted
13 May 2026
Registered enrollment
160
Registry id
NCT05677971

Cross-registrations

EU-CTR / CTIS (EudraCT)2022-501943-34-00

Source: ClinicalTrials.gov, via the CTTI AACT database, data as of 12 Jul 2026. Registry facts are shown as registered by the study sponsor; findmyKOL does not interpret them.